Pane, Marika
Donati, Maria Alice
Cutrona, Costanza
De Sanctis, Roberto
Pirinu, Matteo
Coratti, Giorgia
Ricci, Martina
Palermo, Concetta
Berti, Beatrice
Leone, Daniela
Ticci, Chiara
Sacchini, Michele
Cerboneschi, Margherita
Capasso, Anna
Cicala, Gianpaolo
Pera, Maria Carmela
Bravetti, Chiara
Abiusi, Emanuela
Vaisfeld, Alessandro
Vento, Giovanni
Tiziano, Francesco Danilo
Mercuri, Eugenio
Article History
Received: 8 February 2022
Revised: 31 March 2022
Accepted: 5 April 2022
First Online: 6 May 2022
Change Date: 24 August 2022
Change Type: Update
Change Details: Missing Open Access funding information has been added in the Funding Note.
Declarations
:
: The study was approved by the ethics committee in each center (Policlinico Gemelli, Rome, and Meyer Children’s Hospital, Florence).
: Informed consent was obtained from the parents of all participants included in the study.
: Informed consent was obtained from the parents of all participants included in the study.
: Pane M, Donati MA, De Sanctis R, Coratti G, Tiziano FD, and Mercuri E report personal fees from BIOGEN S.R.L. outside the submitted work; Coratti G, Pera MC, Tiziano FD, and Mercuri E report personal fees from ROCHE outside the submitted work; Pane M, De Sanctis R, Coratti G, and Mercuri E report from personal fees AVEXIS and NOVARTIS outside the submitted work; Tiziano FD report from personal fees NOVARTIS outside the submitted work; Pane M and Mercuri E report personal fees from PTC THERAPEUTICS and SAREPTA outside the submitted work; Coratti G report personal fees from GENESIS PHARMA and Biologix outside the submitted work; Mercuri E report from personal fees SANTHERA outside the submitted work; Cutrona C, Pirinu M, Ricci M, Palermo C, Berti B, Leone D, Ticci C, Sacchini M, Cerboneschi M, Capasso A, Cicala G, Bravetti C, Abiusi E, Vaisfeld A, and Vento G have nothing to disclose.