Abukhaled, Musaad
Al Muqbil, Mohammed
Alghamdi, Malak Ali
Hundallah, Khalid
Suleiman, Jehan http://orcid.org/0000-0003-0914-7650
Ben-Omran, Tawfeg
Alfadhel, Majid
Almannai, Mohammed
Alsaleh, Rehab
Tabarki, Brahim
Article History
Received: 21 September 2022
Revised: 15 February 2023
Accepted: 16 February 2023
First Online: 16 March 2023
Change Date: 4 May 2023
Change Type: Correction
Change Details: A Correction to this paper has been published:
Change Details: https://doi.org/10.1007/s00431-023-05012-1
Declarations
:
: We would like to thank the patients and their families for their assent/consent for their cases to be discussed in this manuscript.
: Musaad Abukhaled, Mohammed Al Muqbil, Jehan Suleiman, Tawfeg Ben-Omran, Majid Alfadhel, and Brahim Tabarki have received honoraria for advisory board meetings from PTC Therapeutics. Malak Alghamdi, Khalid Hundallah, Rehab Alsaleh, and Mohammed Almannai have no disclosures to declare.