Hendriksz, Christian J.
Berger, Kenneth I.
Parini, Rossella
AlSayed, Moeenaldeen D.
Raiman, Julian
Giugliani, Roberto
Mitchell, John J.
Burton, Barbara K.
Guelbert, Norberto
Stewart, Fiona
Hughes, Derralynn A.
Matousek, Robert
Jurecki, Elaina
Decker, Celeste
Harmatz, Paul R.
Funding for this research was provided by:
Fondazione Pierfranco e Luisa Mariani
National Center for Advancing Translational Sciences (UL1 TR000004)
BioMarin Pharmaceutical