Treatment with pentosan polysulphate in patients with MPS I: results from an open label, randomized, monocentric phase II study
Crossref DOI link: https://doi.org/10.1007/s10545-016-9974-5
Published Online: 2016-09-02
Published Print: 2016-11
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Hennermann, Julia B.
Gökce, Seyfullah
Solyom, Alexander
Mengel, Eugen
Schuchman, Edward H.
Simonaro, Calogera M.
Funding for this research was provided by:
Multiplex Pharma Holdings, Miami Beach, FL, USA
Version of Record valid from 2016-09-02
License valid from 2016-09-02