Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I
Crossref DOI link: https://doi.org/10.1007/s10545-017-0052-4
Published Online: 2017-05-30
Published Print: 2017-07
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Penati, Rachele
Fumagalli, Francesca
Calbi, Valeria
Bernardo, Maria Ester
Aiuti, Alessandro
Funding for this research was provided by:
Fondazione Telethon
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License valid from 2017-05-30