Amodru, V.
Sahakian, N.
Piazzola, C.
Appay, R.
Graillon, T.
Cuny, T.
Morange, I.
Albarel, F.
Vermalle, M.
Regis, J.
Dufour, H.
Brue, T.
Castinetti, F. http://orcid.org/0000-0002-1808-8800
Article History
Accepted: 16 February 2024
First Online: 23 March 2024
Declarations
:
: Thierry Brue has received conference/consultancy fees and/or research grants from Association Française contre les Myopathies (AFM Telethon), Ipsen, Lilly, Novartis, Novo-Nordisk, Pfizer and Recordati, and served as clinical trial investigator for Crinetics, Debiopharm, Recordati and Xeris. Frederic Castinetti has received conference/consultancy fees and/or research grants from Ipsen, Recordati rare diseases, and served as clinical trial investigator for Recordati rare diseases.