Dabbous, Omar
Maru, Benit
Jansen, Jeroen P.
Lorenzi, Maria
Cloutier, Martin
Guérin, Annie
Pivneva, Irina
Wu, Eric Q.
Arjunji, Ramesh
Feltner, Douglas
Sproule, Douglas M.
Funding for this research was provided by:
AveXis
Article History
Received: 14 December 2018
First Online: 16 March 2019