Kohlschütter, Alfried http://orcid.org/0000-0002-2700-0401
Schulz, Angela
Bartsch, Udo
Storch, Stephan http://orcid.org/0000-0002-8807-5917
Article History
First Online: 15 March 2019
Compliance with Ethical Standards
:
: No sources of funding were received for the preparation of this review. The Open Access fee was paid from scientific overhead costs awarded to Dr. Angela Schulz.
: Alfried Kohlschütter and Angela Schulz have been consultants to BioMarin Pharmaceutical Inc., Novato, CA, USA during a clinical trial of cerliponase A and have received fees, honoraria, and travel support. Stephan Storch and Udo Bartsch have no conflicts of interest that are directly relevant to the content of this review.