van Ginkel, Willem G.
Rodenburg, Iris L.
Harding, Cary O.
Hollak, Carla E. M.
Heiner-Fokkema, M. Rebecca
van Spronsen, Francjan J.
Article History
First Online: 31 October 2019
Compliance with ethical standards
:
: No external funding was secured for this study.
: ILR has received research grants from SOBI. CEMH is involved in pre-marketing studies with Sanofi, Protalix, and Idorsia in the field of lysosomal storage disorders. She is advisor for drug regulatory agencies and a member of the Advisory Committee to the insurance package of the National Heath Care Institute. FJvS has received research grants, advisory board fees, and speakers honoraria from Nutricia Research, Merck-Serono, Biomarin, Codexis, Alexion, Vitaflo, MendeliKABS, Promethera, SOBI, APR, ARLA Foods Int., Eurocept, Lucane, nestle-Codexis Alliance, Orphan Europe, Rivium Medical BV, Origin, Agios, NPKUA, ESPKU, NPKUV, Tyrosinemia Foundation and Pluvia Biotech. WGvG, COH and MRHF have indicated that they have no potential conflicts of interest to disclose.