Bezzerri, Valentino http://orcid.org/0000-0002-6849-4487
Cipolli, Marco http://orcid.org/0000-0001-6646-421X
Funding for this research was provided by:
Associazione Italiana Sindrome di Shwachman (AISS-2017)
Ministero della Salute (GR-2016-02363570)
Article History
First Online: 9 November 2018
Compliance with Ethical Standards
:
: VB and MC are the inventors of the specific use of ataluren in SDS (patent provisional number 62/393,747 USA).
: This review was supported by the “Associazione Italiana Sindrome di Shwachman” (Grant #AISS-2017 to MC and VB) and the Italian Ministry of Health (Grant GR-2016-02363570 to VB).