Muenzer, Joseph
Hendriksz, Christian J.
Fan, Zheng
Vijayaraghavan, Suresh
Perry, Victor
Santra, Saikat
Solanki, Guirish A.
Mascelli, Mary Ann
Pan, Luying
Wang, Nan
Sciarappa, Kenneth
Barbier, Ann J.
This article is maintained by: Elsevier
Article Title: A phase I/II study of intrathecal idursulfase-IT in children with severe mucopolysaccharidosis II
Journal Title: Genetics in Medicine
CrossRef DOI link to publisher maintained version: https://doi.org/10.1038/gim.2015.36
Content Type: article
Copyright: © 2016, The Author(s), under exclusive licence to the American College of Medical Genetics and Genomics