Han, Lijie
Gan, Lina
Schäfer, Balázs
Voss, Dillon M.
Danielsen, Mathias
Kostov, Ondrej https://orcid.org/0000-0002-0194-1852
Liu, Jia
Wang, Ting
Caruthers, Marvin H.
Chen, Hao
Krainer, Adrian R. https://orcid.org/0000-0001-9024-9501
Article History
Received: 24 August 2025
Accepted: 20 February 2026
First Online: 21 April 2026
Competing interests
: A.R.K. discloses the following commercial relationships, unrelated to the present work: Stoke Therapeutics (Co-Founder and Director); SABs of Inverna Therapeutics, Saturnus Bio, and Autoimmunity BioSolutions; and Consultant for Biogen, SEED Therapeutics, Crucible Therapeutics, Cajal Neuroscience, and Collage Bio. M.H.C. discloses the following commercial interests, unrelated to the current work: ProGenis Therapeutics (Co-Founder and Director), Cirena (Co-Founder and Director), LincSwitch (Director and SAB), SynGenis (Director), SABs of Veranova and Vesicle Therapeutics.