Heneghan, Sophia https://orcid.org/0000-0002-4467-3499
Elhassan, Elhussein A. E.
Ghani, Hamidah
Collins, Kane
Teltsh, Omri
Conlon, Peter J. https://orcid.org/0000-0001-6772-9531
Benson, Katherine A.
Cavalleri, Gianpiero L. https://orcid.org/0000-0002-9802-0506
Funding for this research was provided by:
Science Foundation Ireland (18/CRT/6214)
Science Foundation Ireland (18/CRT/6214)
Science Foundation Ireland (18/CRT/6214)
Science Foundation Ireland (18/CRT/6214)
BioMarin Pharmaceutical
Article History
Received: 7 July 2025
Revised: 5 November 2025
Accepted: 20 January 2026
First Online: 18 February 2026
Competing interests
: This publication has emanated from research supported by BioMarin Pharmaceutical Inc.
: This study was approved by Beaumont Hospital Ethics Committee under protocol 19/23 and was conducted according to the Declaration of Helsinki. All participants provided informed, written consent.