Sanders, Francis W. B. https://orcid.org/0000-0003-1625-7487
Votruba, Marcela https://orcid.org/0000-0002-7680-9135
Article History
Received: 16 April 2025
Revised: 18 August 2025
Accepted: 2 September 2025
First Online: 17 September 2025
Competing interests
: Neither MV nor FS has any competing interests to declare regarding the present manuscript. MV received consultation fees from Santhera Pharmaceuticals, Chiesi Farmaceutici and Stoke Therapeutics.