Nafchi, Neda A. M. https://orcid.org/0000-0003-0714-7403
Chilcott, Ellie M.
Brown, Sharon https://orcid.org/0000-0001-9671-7054
Fuller, Heidi R.
Bowerman, Melissa https://orcid.org/0000-0002-3579-6403
Yáñez-Muñoz, Rafael J. https://orcid.org/0000-0001-7113-1938
Funding for this research was provided by:
Spinal Muscular Atrophy Trust (UK SMA Research Consortium)
SMA UK
SMA Trust (UK SMA Research Consortium, UK SMA Research Consortium)
Royal Holloway University of London
Royal Holloway University of London
Great Ormond Street Hospital Charity (V5018, V5018)
Muscular Dystrophy UK
Action Medical Research
Academy of Medical Sciences
SMA UK (reference: UK SMA Research Consortium) SMA Angels Charity
Article History
Received: 20 April 2022
Revised: 14 April 2023
Accepted: 4 May 2023
First Online: 15 June 2023
Competing interests
: NAMN, EMC, and RJY-M have filed a patent application on the uses of the novel SMN transgene reported in this manuscript. SB, HRF, and MB report no conflicts of interest.