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Intrathecal enzyme replacement for Hurler syndrome: biomarker association with neurocognitive outcomes

Crossref DOI link: https://doi.org/10.1038/s41436-019-0522-1

Published Print: 2019-11

Update policy: https://doi.org/10.1016/elsevier_cm_policy

Authors

Eisengart, Julie B.

Pierpont, Elizabeth I.

Kaizer, Alexander M.

Rudser, Kyle D.

King, Kelly E.

Pasquali, Marzia

Polgreen, Lynda E.

Dickson, Patricia I.

Le, Steven Q.

Miller, Weston P.

Tolar, Jakub

Orchard, Paul J.

Lund, Troy C.
Funding

Funding for this research was provided by:

National Institute of Neurological Disorders and Stroke (U54NS065768)

National Center for Advancing Translational Sciences (UL1TR002494)

Sanofi Genzyme (NA)

Children's Cancer Research Fund (CCRF)
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Text and Data Mining valid from 2019-11-01

Text and Data Mining valid from 2019-11-01

Version of Record valid from 2021-11-24
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This article is maintained by: Elsevier

Article Title: Intrathecal enzyme replacement for Hurler syndrome: biomarker association with neurocognitive outcomes

Journal Title: Genetics in Medicine

CrossRef DOI link to publisher maintained version: https://doi.org/10.1038/s41436-019-0522-1

Content Type: article

Copyright: © 2019, The Author(s), under exclusive licence to the American College of Medical Genetics and Genomics