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Authors
Rai, Rajeev
Romito, Marianna
Rivers, Elizabeth
Turchiano, Giandomenico
Blattner, Georges
Vetharoy, Winston
Ladon, Dariusz
Andrieux, Geoffroy
Zhang, Fang
Zinicola, Marta
Leon-Rico, Diego
Santilli, Giorgia http://orcid.org/0000-0003-1776-1984
Thrasher, Adrian J. http://orcid.org/0000-0002-6097-6115
Cavazza, Alessia http://orcid.org/0000-0002-4735-2121
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Funding
Funding for this research was provided by:
Wellcome Trust (104807/Z/14/Z)
NIHR Biomedical Research Centre at Great Ormond Street Hospital for Children NHS Foundation Trust and University College London. University College London Therapeutic Acceleration Support fund.
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Article History
Received: 26 September 2019
Accepted: 3 July 2020
First Online: 12 August 2020
Competing interests
: A.J.T is on the Scientific Advisory Board of Orchard Therapeutics and Rocket Pharmaceuticals. The other authors declare no competing interests.
