Miskalis, Angelo
Shirguppe, Shraddha
Winter, Jackson
Elias, Gianna
Swami, Devyani
Nambiar, Ananthan https://orcid.org/0000-0002-9767-9456
Stilger, Michelle
Woods, Wendy S.
Gosstola, Nicholas
Gapinske, Michael
Zeballos, Alejandra https://orcid.org/0000-0002-5194-2909
Moore, Hayden
Maslov, Sergei https://orcid.org/0000-0002-3701-492X
Gaj, Thomas https://orcid.org/0000-0001-6004-9664
Perez-Pinera, Pablo https://orcid.org/0000-0002-9167-0004
Funding for this research was provided by:
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (1U01NS122102, 1R01NS123556, 1U01NS122102, 1R01NS123556)
U.S. Department of Health & Human Services | NIH | National Institute of General Medical Sciences (1R01GM141296, 1R01GM127497, 1R01GM131272, 1R01GM141296)
Muscular Dystrophy Association (MDA602798, MDA602798)
American Heart Association (17SDG33650087)
Article History
Received: 15 December 2023
Accepted: 13 November 2024
First Online: 28 November 2024
Competing interests
: P.P.P., M.G., and J.W. are named inventors in pending patent application US17/260,828 filed by the University of Illinois. Methods for exon skipping and AAV-mediated delivery of base editors are covered in the patent application. The remaining authors declare no competing interests.