Notaro, Marco https://orcid.org/0000-0003-4328-4835
Borghetti, Maristella
Bresesti, Chiara https://orcid.org/0000-0002-1840-9774
Giacca, Giovanna
Kerzel, Thomas https://orcid.org/0000-0003-0763-5319
Mercado, Carl Mirko https://orcid.org/0009-0000-9599-9563
Beretta, Stefano https://orcid.org/0000-0003-4375-004X
Monti, Marco https://orcid.org/0000-0003-1266-4325
Merelli, Ivan
Iaia, Silvia
Genua, Marco https://orcid.org/0000-0002-0764-8163
Annoni, Andrea https://orcid.org/0000-0002-8541-2578
Canu, Tamara
Cristofori, Patrizia
Degl’Innocenti, Sara
Sanvito, Francesca https://orcid.org/0000-0002-4046-8420
Rancoita, Paola Maria Vittoria
Ostuni, Renato https://orcid.org/0000-0003-0460-3426
Gregori, Silvia https://orcid.org/0000-0002-3517-9683
Naldini, Luigi https://orcid.org/0000-0002-7835-527X
Squadrito, Mario Leonardo https://orcid.org/0000-0002-1188-0299
Article History
Received: 19 July 2024
Accepted: 18 March 2025
First Online: 11 April 2025
Competing interests
: M.L.S., L.N., M.N., and T.K. are inventors on a patent on KC-directed gene transfer, and L.N. is an inventor on patents on miRNA-regulated LV technology filed and managed by the San Raffaele Scientific Institute and the Telethon Foundation. The remaining authors declare no competing interests.