Goret, Marie https://orcid.org/0000-0002-9686-5476
Edelweiss, Evelina
Jehl, Jérémy
Reiss, David
Aguirre-Pineda, Patricio https://orcid.org/0009-0006-4869-8681
Friant, Sylvie https://orcid.org/0000-0002-5412-6288
Laporte, Jocelyn https://orcid.org/0000-0001-8256-5862
Article History
Received: 7 June 2024
Accepted: 2 May 2025
First Online: 20 May 2025
Competing interests
: JL patented DNM2 downregulation for centronuclear myopathy treatment. The remaining authors declare no competing interests.