Farnaes, Lauge
Hildreth, Amber
Sweeney, Nathaly M.
Clark, Michelle M.
Chowdhury, Shimul
Nahas, Shareef
Cakici, Julie A. https://orcid.org/0000-0001-5672-3396
Benson, Wendy
Kaplan, Robert H.
Kronick, Richard
Bainbridge, Matthew N.
Friedman, Jennifer
Gold, Jeffrey J.
Ding, Yan
Veeraraghavan, Narayanan
Dimmock, David
Kingsmore, Stephen F.
Article History
Received: 18 January 2018
Revised: 6 March 2018
Accepted: 12 March 2018
First Online: 4 April 2018
Competing interests
: Dr Dimmock declares the following potential conflicts of interest: Biomarin (Consultant for Pegvaliase trials) Audentes Therapeutics (Scientific Advisory Board).