Babai, Arwa
Oliveira, Daniela
Gialeli, Andriana
Drozniewska, Malgorzata
Kainov, Yaroslav
Dias, Cristina
Funding for this research was provided by:
Research Mobility Fellowship 2022 - ERN Rare Disease Training and Support Program - European Joint Programme on Rare Diseases (EJP RD COFUND-EJP N°825575)
Great Ormond Street Hospital Charity (V4723)
Guy’s & St Thomas’ Charity (STR111001)
Friends of Guy’s & St Thomas’ Hospital (23/03R)
Article History
Received: 18 March 2025
Accepted: 4 July 2025
First Online: 21 October 2025
Competing interests
: The authors declare no competing interests.