Jones, Brendan C. https://orcid.org/0000-0002-2637-8859
Benedetti, Giada https://orcid.org/0000-0002-6852-9993
CalĂ , Giuseppe https://orcid.org/0000-0003-2297-700X
Amiri, Ramin https://orcid.org/0000-0002-2455-0707
Tullie, Lucinda https://orcid.org/0000-0001-5679-7504
Lutman, Roberto
Sufi, Jahangir https://orcid.org/0000-0002-4563-5531
Holland, Lucy
Jafree, Daniyal J. https://orcid.org/0000-0001-8235-0394
Balys, Monika
Anderson, Glenn
Simcock, Ian C. https://orcid.org/0000-0002-5619-0785
Arthurs, Owen J. https://orcid.org/0000-0003-1213-3516
Eaton, Simon https://orcid.org/0000-0003-0892-9204
Elvassore, Nicola https://orcid.org/0000-0002-7029-6287
Li, Vivian SW
Tape, Christopher J. https://orcid.org/0000-0003-4712-2737
Jones, Kelsey DJ
Luni, Camilla https://orcid.org/0000-0002-1211-9629
Giobbe, Giovanni Giuseppe https://orcid.org/0000-0001-6958-7303
De Coppi, Paolo https://orcid.org/0000-0002-1659-0207
Funding for this research was provided by:
Oak Foundation (W1095/OCAY-14-191)
Great Ormond Street Hospital Charity (VS2606)
DH | National Institute for Health Research
Rosetrees Trust (Seedcorn2025\100314)
UCL Therapeutic Acceleration Support (TAS) LifeArc Fund Rare Diseases Call
Article History
Received: 1 May 2024
Accepted: 1 October 2025
First Online: 23 January 2026
Competing interests
: The authors declare no competing interests.