Khoury, Michael https://orcid.org/0000-0001-6112-6860
Ware, Adam L. https://orcid.org/0000-0002-3990-5734
McCrindle, Brian W. https://orcid.org/0000-0001-6485-6551
Article History
Accepted: 27 August 2025
First Online: 12 September 2025
Competing interests
: M.K. is on the advisory board of Ultragenyx and is a site investigator for Esperion. A.L.W. is a site investigator for Esperion and Novartis. B.W.M. is a consultant for Amryt Pharma, Chiesi, Esperion, J&J and Ultragenyx, and is a site investigator for Esperion.