Document is current
Any future updates will be listed below
-
Authors
Scotti, Celeste
Aiuti, Alessandro https://orcid.org/0000-0002-5398-1717
Naldini, Luigi https://orcid.org/0000-0002-7835-527X
- License Information
-
More Information
Article History
First Online: 10 March 2025
Competing interests
: C.S. is the director of research and development at Fondazione Telethon, which is the marketing authorization holder for Strimvelis. A.A. is a principal investigator of clinical trials for rare genetic diseases sponsored by Orchard Therapeutics or Fondazione Telethon. L.N. is the inventor on several patents on lentiviral vector–mediated gene therapy.
