Bello, Luca http://orcid.org/0000-0002-3075-6525
Hoffman, Eric P.
Pegoraro, Elena http://orcid.org/0000-0002-7740-4156
Article History
Accepted: 11 May 2023
First Online: 12 June 2023
Competing interests
: L.B. reports honoraria (speaker, advisory boards) from PTC Therapeutics, Sarepta Therapeutics, Edgewise Therapeutics, Epirium Bio and research funding from PTC Therapeutics. E.P.H. reports salary support from Reveragen and AGADA Biosciences. E.P. reports personal fees from Sarepta, grants and non-financial support from Santhera, personal fees and non-financial support from PTC Pharmaceuticals, non-financial support from Genzyme and personal fees from Roche, outside the submitted work.