Ziółkowska, Ewa A. https://orcid.org/0000-0003-1822-3133
Takahashi, Keigo https://orcid.org/0000-0003-2183-068X
Dickson, Patricia I. https://orcid.org/0000-0003-3467-8488
Sardiello, Marco https://orcid.org/0000-0001-6484-0250
Sands, Mark S. https://orcid.org/0000-0002-5559-0832
Cooper, Jonathan D. https://orcid.org/0000-0003-1339-4750
Article History
Accepted: 8 August 2025
First Online: 4 September 2025
Competing interests
: J.D.C. has received research support from Abeona Therapeutics Inc., BioMarin Pharmaceutical Inc., Neurogene, and REGENXBIO Inc. and is a consultant for JCR Pharmaceuticals. The remaining authors declare no conflicts of interest.