Sadler, Freja https://orcid.org/0009-0004-7637-5041
Tabrizi, Sarah J. https://orcid.org/0000-0003-2716-2045
Article History
First Online: 26 May 2026
Competing interests
: S.J.T. reports that fees for advisory services were paid to University College London Consultants, a wholly owned subsidiary of University College London (UCL), from Alnylam Pharmaceuticals and UniQure Biopharma. UCL Hospitals NHS Foundation Trust, S.J.T.’s host clinical institution, received funding to run clinical trials for Alnylam Pharmaceuticals and UniQure Biopharma. F.S. declares no competing interests.