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Article History
Received: 11 April 2023
Accepted: 2 May 2024
First Online: 4 September 2024
Competing interests
: R.D.S. has been a consultant for Leadiant Biosciences, Mirum Pharmaceuticals, PTC Therapeutics and Travere. He has received honoraria from Medscape and is an employee and shareholder of PreventionGenetics, part of Exact Sciences. B.P.K. is a co-inventor on patents and patent applications that describe genome engineering technologies, and is on the scientific advisory board of Acrigen Biosciences, Life Edit Therapeutics and Prime Medicine. The other authors declare no competing interests.