Fong, Sylvia http://orcid.org/0000-0002-3818-4146
Yates, Bridget
Sihn, Choong-Ryoul
Mattis, Aras N.
Mitchell, Nina
Liu, Su
Russell, Chris B. http://orcid.org/0000-0002-0240-1815
Kim, Benjamin
Lawal, Adebayo
Rangarajan, Savita http://orcid.org/0000-0001-7367-133X
Lester, Will
Bunting, Stuart
Pierce, Glenn F.
Pasi, K. John
Wong, Wing Yen
Funding for this research was provided by:
BioMarin Pharmaceutical
Article History
Received: 29 April 2021
Accepted: 17 February 2022
First Online: 11 April 2022
Competing interests
: S.F., B.Y., C.-R.S., N.M., S.L., C.B.R., B.K., A.L., S.B. and W.Y.W. are full-time employees of BioMarin Pharmaceutical and hold stock in BioMarin Pharmaceutical. A.N.M. receives consulting fees from Ambys Medicines, BioMarin Pharmaceutical, HEPATX and Pliant. S.R. reports being an advisory board member for Pfizer, Sanofi, Sigilon and Takeda; receiving conference support from Reliance Life Sciences and Shire/Takeda; and receiving consulting fees from Reliance Life Sciences. G.F.P. reports receiving consulting fees from Ambys Medicines, BioMarin Pharmaceutical, Decibel Therapeutics, Frontera, Intellia, Pfizer, Regeneron, Spark and Third Rock Ventures, and is employed by Voyager Therapeutics. K.J.P. reports receiving consulting fees from Alnylam, Apcintex, BioMarin Pharmaceutical, Bioverativ, Catalyst Bio, Catapult, Chugai, Novo Nordisk, Roche, Sanofi and Sobi; participating as an investigator for BioMarin Pharmaceutical, Sanofi and uniQure; receiving speaker fees from Bayer, BioMarin Pharmaceutical, Biotest, Novo Nordisk, Octapharma, Pfizer, Sanofi, Shire, Sobi and uniQure; and receiving travel support from Alnylam, BioMarin Pharmaceutical, Bayer, Bioverativ, Novo Nordisk, Octapharma, Pfizer, Shire and Sobi. W.L. reports receiving consulting fees from Novo Nordisk, Octapharma and Takeda; participating as an investigator for BioMarin Pharmaceutical; receiving speaker fees from Novo Nordisk, CSL Behring, Sobi and Takeda; and receiving travel support from CSL Behring, Novo Nordisk and Takeda.