Prat-Ortega, GenĂs https://orcid.org/0000-0002-3401-3569
Ensel, Scott
Donadio, Serena
Borda, Luigi https://orcid.org/0009-0003-4670-8530
Boos, Amy
Yadav, Prakarsh
Verma, Nikhil https://orcid.org/0009-0004-5533-6887
Ho, Jonathan
Carranza, Erick
Frazier-Kim, Sarah https://orcid.org/0009-0004-8558-1883
Fields, Daryl P.
Fisher, Lee E. https://orcid.org/0000-0002-9072-3119
Weber, Doug J. https://orcid.org/0000-0002-9782-3497
Balzer, Jeffrey
Duong, Tina
Weinstein, Steven D.
Eliasson, Mikael J. L.
Montes, Jacqueline https://orcid.org/0000-0002-7357-0819
Chen, Karen S.
Clemens, Paula R. https://orcid.org/0000-0002-0652-6703
Gerszten, Peter
Mentis, George Z.
Pirondini, Elvira https://orcid.org/0000-0002-8078-3951
Friedlander, Robert M. https://orcid.org/0000-0002-5008-7592
Capogrosso, Marco https://orcid.org/0000-0002-0975-316X
Funding for this research was provided by:
Hoffman-La Roche, research grant number SRA1898
SMA Foundation and SMA Europe doctoral fellowship SRA4272
Article History
Received: 1 October 2024
Accepted: 20 December 2024
First Online: 5 February 2025
Competing interests
: This study was supported by an exploratory research grant from F. Hoffmann-La Roche to M.C., and Genentech and the University of Pittsburgh hold rights to intellectual property related to this study. M.C., G.P.O. and M.J.L.E. hold patent applications that relate to this work. The remaining authors declare no competing interests.