Molteni, Raffaella https://orcid.org/0000-0001-6605-2346
Fiumara, Martina https://orcid.org/0009-0007-5934-9273
Campochiaro, Corrado
Alfieri, Roberta https://orcid.org/0000-0001-6922-9696
Pacini, Guido
Licari, Eugenia
Tomelleri, Alessandro
Diral, Elisa
Varesi, Angelica
Weber, Alessandra
Quaranta, Pamela
Albano, Luisa https://orcid.org/0000-0002-0013-4741
Gaddoni, Chiara
Basso-Ricci, Luca
Stefanoni, Davide
Alessandrini, Laura
Degl’Innocenti, Sara
Sanvito, Francesca https://orcid.org/0000-0002-4046-8420
Bergonzi, Gregorio Maria https://orcid.org/0009-0007-1339-2663
Annoni, Andrea https://orcid.org/0000-0002-8541-2578
Panigada, Maddalena
Cantoni, Eleonora
Canarutto, Daniele https://orcid.org/0000-0001-6999-8479
Xie, Stephanie Z. https://orcid.org/0000-0002-0284-494X
D’Alessandro, Angelo https://orcid.org/0000-0002-2258-6490
Di Micco, Raffaella https://orcid.org/0000-0002-0639-8238
Aiuti, Alessandro https://orcid.org/0000-0002-5398-1717
Ciceri, Fabio https://orcid.org/0000-0003-0873-0123
De Luca, Giacomo
Dagna, Lorenzo https://orcid.org/0000-0002-7428-315X
Matucci-Cerinic, Marco
Merelli, Ivan
Cenci, Simone https://orcid.org/0000-0003-1215-7518
Scala, Serena
Cavalli, Giulio
Naldini, Luigi https://orcid.org/0000-0002-7835-527X
Ferrari, Samuele https://orcid.org/0000-0003-1122-1231
Funding for this research was provided by:
American Society of Hematology (2024 ASH Global Research Award)
Fondazione Telethon (SR-Tiget Core Grant, SR-Tiget Core Grant, SR-Tiget Core Grant)
Else Kröner-Fresenius-Stiftung (Prize)
Ministero dell'Istruzione, dell'Università e della Ricerca (2022APWTE3, 2022APWTE3, 2022APWTE3)
Ministero della Salute (GR-2019-12369499)
Article History
Received: 8 July 2024
Accepted: 28 February 2025
First Online: 7 April 2025
Competing interests
: S.F., L.N., M.F., D.C., A.W. and R.D.M. are inventors of patents on HSPC gene editing. R.M., M.F., G.C., L.N. and S.F. are inventors of patents on VEXAS syndrome. All patents are owned and managed by the San Raffaele Scientific Institute and the Telethon Foundation. L.N. is a founder, quota holder and consultant of GeneSpire and Chroma Medicine. G.C. is currently an employee of Novartis. The other authors declare no competing interests.