Wagner, Matias https://orcid.org/0000-0002-4454-8823
Berecki, Géza https://orcid.org/0000-0002-8664-6325
Fazeli, Walid
Nussbaum, Claudia
Flemmer, Andreas W. https://orcid.org/0000-0002-4601-0314
Frizzo, Silvana
Heer, Farina
Heinen, Florian https://orcid.org/0000-0002-3872-6136
Horton, Robert
Jacotin, Henry
Motel, William
Spar, Brian
Klein, Christoph https://orcid.org/0000-0003-0956-0445
Siegel, Corinna
Hübener, Christoph
Stöcklein, Sophia
Paolini, Marco
Staudt, Martin
Tacke, Moritz
Wolff, Markus
Petrou, Steven
Souza, Marcio https://orcid.org/0009-0004-6392-5104
Borggraefe, Ingo https://orcid.org/0000-0002-8484-5945
Funding for this research was provided by:
Gemeinnützige Hertie-Stiftung (P1230037)
Article History
Received: 24 September 2024
Accepted: 14 March 2025
First Online: 22 April 2025
Competing interests
: Elsunersen was provided by Praxis Precision Medicines within an expanded access program with authors being employees of Praxis Precision Medicines (S.F., R.H., H.J., W.M., B.S., S.P. and M.So.). The other authors declare no competing interests.