Kaeser, Stephan A. https://orcid.org/0000-0002-4188-5111
Schultz, Stephanie A. https://orcid.org/0000-0001-8460-4415
Hofmann, Anna
Häsler, Lisa M.
Xu, Ying https://orcid.org/0009-0002-3728-6519
Lambert, Marius
Obermüller, Ulrike
Brockmann, Kathrin https://orcid.org/0000-0002-7515-8596
Bijzet, Johan https://orcid.org/0000-0002-0375-4460
Nienhuis, Hans https://orcid.org/0000-0003-3974-6830
Nuvolone, Mario https://orcid.org/0000-0001-8334-1684
Obici, Laura
Palladini, Giovanni https://orcid.org/0000-0001-5994-5138
Hegenbart, Ute https://orcid.org/0000-0003-1917-6746
Schönland, Stefan O. https://orcid.org/0000-0002-4853-5579
Jucker, Mathias https://orcid.org/0000-0001-9045-1072
Funding for this research was provided by:
European Joint Program for Rare Diseases
Article History
Received: 25 June 2025
Accepted: 5 February 2026
First Online: 11 March 2026
Competing interests
: The authors declare no competing interests.