Rodriguez, Caitlin M.
Wright, Shannon E.
Kearse, Michael G.
Haenfler, Jill M.
Flores, Brittany N.
Liu, Yu
Ifrim, Marius F.
Glineburg, Mary R.
Krans, Amy
Jafar-Nejad, Paymaan
Sutton, Michael A.
Bassell, Gary J. https://orcid.org/0000-0003-2622-0127
Parent, Jack M. https://orcid.org/0000-0002-2972-1528
Rigo, Frank
Barmada, Sami J. https://orcid.org/0000-0002-9604-968X
Todd, Peter K. https://orcid.org/0000-0003-4781-6376
Funding for this research was provided by:
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (F31 NS090883)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (T32-NS076401)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (F32NS089124)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (T32NS007222)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (R01NS097542)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (P30AG053760)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (P30NS05507708)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (T32NS007222)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (P30NS05507708)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (P30AG053760)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (R01NS097542)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (R01NS099280)
U.S. Department of Health & Human Services | NIH | National Institute of Neurological Disorders and Stroke (R01NS086810)
U.S. Department of Health & Human Services | NIH | National Institute of General Medical Sciences (K99GM126064)
FRAXA Research Foundation
Ionis Pharmaceuticals
Article History
Received: 8 October 2018
Accepted: 10 January 2020
First Online: 17 February 2020
Competing interests
: P.K.T. served as a consultant with Denali Therapeutics and has licensed technology through the University of Michigan to Denali. P.K.T., C.M.R., F.R. and P.J. hold a patent on ASOs targeting CGG RAN. F.R. and P.J. are paid employees of Ionis Pharmaceuticals. All other authors declare no competing interests.