Mittas, David M. https://orcid.org/0009-0006-9554-3033
Riedmayr, Lisa M.
Gavrilov, Zoran
Weber, Valentin J. https://orcid.org/0009-0004-9354-5014
Otify, Dina Y.
Mehlfeld, Verena
Szalontai, Balint https://orcid.org/0000-0001-6421-2553
Ucambarlic, Emina
Gandor, Catharina https://orcid.org/0009-0009-7660-3485
Heigl, Thomas https://orcid.org/0000-0003-1571-8579
Biel, Martin
Becirovic, Elvir
Funding for this research was provided by:
Schweizerischer Nationalfonds zur Förderung der Wissenschaftlichen Forschung (320030E_221942 & 310030_212190)
Deutsche Forschungsgemeinschaft (513025799/FOR5621, 513025799/FOR5621)
University Research Priority Program of the University of Zurich (URPP) ITINERARE – Innovative Therapies in Rare Diseases
Article History
Received: 28 February 2025
Accepted: 26 June 2025
First Online: 11 September 2025
Competing interests
: E.B. and M.B. are authors on a patent application covering the splice site module and its applications (PCT/EP2019/086454, filed by ViGeneron GmbH, status: published). The other authors declare no competing interests.