LNA/DNA mixmer-based antisense oligonucleotides correct alternative splicing of the SMN2 gene and restore SMN protein expression in type 1 SMA fibroblasts
Crossref DOI link: https://doi.org/10.1038/s41598-017-03850-2
Published Online: 2017-06-16
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Touznik, Aleksander
Maruyama, Rika
Hosoki, Kana
Echigoya, Yusuke
Yokota, Toshifumi
Text and Data Mining valid from 2017-06-16
Version of Record valid from 2017-06-16
Article History
Received: 8 July 2016
Accepted: 8 May 2017
First Online: 16 June 2017
Competing Interests
: The authors declare that they have no competing interests.