Aung-Htut, May Thandar
Ham, Kristin A.
Tchan, Michel
Johnsen, Russell
Schnell, Frederick J.
Fletcher, Sue
Wilton, Steve D.
Article History
Received: 6 January 2020
Accepted: 30 March 2020
First Online: 21 April 2020
Competing interests
: S.F. and S.D.W. are consultants for Sarepta Therapeutics, and M.T.A.-H. and K.A.H’s salaries are partly supported by Sarepta Therapeutics. S.F. and S.D.W. are named inventors or contributors on a patent describing the correction of abnormal GAA splicing arising from the c.-32-13T > G variant. F.J.S. is an employee of Sarepta Therapeutics. M.T. and R.J. do not have any conflicting interests.