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Successful skipping of abnormal pseudoexon by antisense oligonucleotides in vitro for a patient with beta-propeller protein-associated neurodegeneration

Crossref DOI link: https://doi.org/10.1038/s41598-024-56704-z

Published Online: 2024-03-18

Update policy: https://doi.org/10.1007/springer_crossmark_policy

Authors

Yamada, Mamiko

Maeta, Kazuhiro

Suzuki, Hisato

Kurosawa, Ryo

Takenouchi, Toshiki

Awaya, Tomonari

Ajiro, Masahiko

Takeuchi, Atsuko

Nishio, Hisahide

Hagiwara, Masatoshi

Miya, Fuyuki

Matsuo, Masafumi

Kosaki, Kenjiro
Funding

Funding for this research was provided by:

JSPS KAKENHI Grant-in-Aid for Early-Career Scientists (21K15873)

Grant-in-Aid for JSPS Fellows (22J23899)

Japan Agency for Medical Research and Development (JP23ek0109672)
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Article History

Received: 28 October 2023

Accepted: 9 March 2024

First Online: 18 March 2024

Competing interests

: The authors declare no competing interests.

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