Document is current

Article History

Received: 16 April 2024

Accepted: 21 August 2024

First Online: 8 October 2024

Competing interests

: ADH is a site principal investigator for clinical research studies sponsored by Astellas, Dyne, Fulcrum, Italafarmaco, MLBio, Novartis, Reveregan/Santhera, and NS Pharma, Inc.; HT reports no conflicts of interest; EM is a principal investigator and consultant (advisory board) for Italfarmaco, Pfizer, PTC, Roche, Santhera, Sarepta, and NS Pharma, Inc.; VS reports no conflicts of interest; LW reports no conflicts of interest; CYA reports no conflicts of interest; MT reports employment for NS Pharma, Inc.; MLP reports employment for NS Pharma, Inc.; RAC reports employment for NS Pharma, Inc.; LM reports employment for NS Pharma, Inc.; PRC reports grants from Amicus, the US Food and Drug Administration, Foundation to Eradicate Duchenne, Hoffman-La Roche, the National Institutes of Health, Sanofi, Spark, and NS Pharma, Inc. and consulting/advisory roles for Catalyst Education and Med Learning Group.