Rezaei, Kimia
Shahraki, Kourosh
Chen, Lauren
Yassin, Shaden H.
Lee, Olivia L.
Shahraki, Kianoush
Suh, Donny W.
Funding for this research was provided by:
Recordati Rare Diseases
Article History
Received: 25 February 2025
Accepted: 12 September 2025
First Online: 16 October 2025
Declarations
:
: The authors declare no competing interests.