Ahmadiharchegani, Fatemeh
Tobin, Rebecca A.
Degan, Chiara
Naveed, Ahmed
Guglieri, Michela
Jiménez-Requena, Albert
de Vries, Sharon I.
Szigyarto, Cristina Al-Khalili
Spitali, Pietro
Tsonaka, Roula
van der Burgt, Yuri E. M.
Diaz-Manera, Jordi
,
Damsker, Jesse M.
Perlman, Seth J.
Smith, Edward C.
Horrocks, Iain
Finkel, Richard S.
Mah, Jean K.
Deconinck, Nicolas
Goemans, Nathalie M.
Haberlová, Jana
Straub, Volker
Mengle-Gaw, Laurel
Schwartz, Benjamin D.
Harper, Amy
Shieh, Perry B.
De Waele, Liesbeth
Castro, Diana
Yang, Michele L.
Ryan, Monique M.
McDonald, Craig M.
Henricson, Erik K.
Goude, Erica
Tulinius, Mar
Webster, Richard I.
Mcmillan, Hugh J.
Kuntz, Nancy
Rao, Vamshi K.
Baranello, Giovanni
Spinty, Stefan
Childs, Anne-Marie
Sbrocchi, Annie M.
Selby, Kathryn A.
Monduy, Migvis
Nevo, Yoram
Vilchez, Juan J.
Nascimento-Osorio, Andres
Niks, Erik H.
De Groot, Imelda JM
Katsalouli, Marina
Van DenAnker, John N.
Ward, Leanne M.
Leinonen, Mika
Duong, Tina
Rocha, Carolina Tesi
Thangarajh, Mathula
D’Alessandro, MD Andrea L.
Morgenroth, Lauren P.
,
Bushby, Kate
McDermott, Michael P.
Hart, Kimberly A.
Tawil, Rabi
Martens, William B.
Herr, Barbara E.
McColl, Elaine
Speed, Chris
Wilkinson, Jennifer
Kirschner, Janbernd
King, Wendy M.
Eagle, Michelle
Brown, Mary W.
Willis, Tracey
Griggs, Robert C.
Straub, Volker
van Ruiten, Henriette
Childs, Anne-Marie
Ciafaloni, Emma
Shieh, Perry B.
Spinty, Stefan
Maggi, Lorenzo
Baranello, Giovanni
Butterfield, Russell J.
Horrocks, IA
Roper, Helen
Alhaswani, Zoya
Flanigan, Kevin M.
Kuntz, Nancy L.
Manzur, Adnan
Darras, Basil T.
Kang, Peter B.
Morrison, Leslie
Krzesniak-Swinarska, Monika
Mah, Jean K.
Mongini, Tiziana E.
Ricci, Federica
von der Hagen, Maja
Finkel, Richard S.
O’Reardon, Kathleen
Wicklund, Matthew
Kumar, Ashutosh
McDonald, Craig M.
Han, Jay J.
Joyce, Nanette
Henricson, Erik K.
Schara-Schmidt, Ulrike
Gangfus, Andrea
Wilichowski, Ekkehard
Barohn, Richard J.
Statland, Jeffrey M.
Campbell, Craig
Vita, Giuseppe
Vita, Gian Luca
FHoward, James
Hughes, Imelda
McMillan, Hugh J.
Pegoraro, Elena
Bello, Luca
Burnette, WBryan
Thangarajh, Mathula
Chang, Taeun
Clemens, Paula R.
Hoffman, Eric P.
Dang, Utkarsh J.
Hathout, Yetrib
Funding for this research was provided by:
NIH NINDS (R61NS119639)
Department of Defense
Foundation to Eradicate Duchenne
Article History
Received: 23 July 2025
Accepted: 8 October 2025
First Online: 14 November 2025
Declarations
:
: UJD has served as an ad-hoc consultant for ReveraGen Biopharma in the past.