Bauman, Taylor A.
Lee, Sean M.
Juel, Vern C.
Li, Yingkai
Gilbert, Karli
Chen, Jiaxin
Kaminski, Henry J.
Kusner, Linda L.
,
Gable, Karissa L.
Ruzhansky, Katherine
Howard, James F. Jr.
Soliven, Betty
Habib, Ali A.
Gandhi Mehta, Rachana K.
Nowak, Richard J.
Funding for this research was provided by:
Rare Disease Clinical Research Network Consortium (NIH U54 NS115054, NIH U54 NS115054, NIH U54 NS115054, NIH U54 NS115054, NIH U54 NS115054, NIH U54 NS115054, NIH U54 NS115054, NIH U54 NS115054)
Article History
Received: 9 October 2024
Accepted: 7 April 2025
First Online: 15 April 2025
Declarations
:
: Y.L. was supported by MGFA High-Impact Pilot Project Awards. H.J.K., V.C.J., Y.L., K.R., B.S., A.A.H., R.K.G.M., R.J.N. are supported by MGNet (RDCRN) NIH U54 NS115054. T.A.B., S.M.L., K.G., J.C., L.L.K., K.L.G., J.F.H. declare no competing interests.