Catalano, Fabio
Stevic, Dejan https://orcid.org/0009-0009-0837-1993
Zundo, Giacomo
Huizer, Tessa F
Dammou, Zina
Vlaar, Eva C
Katsavelis, Drosos https://orcid.org/0000-0001-6841-2210
van den Bosch, Jeroen C
van den Hout, Hannerieke J M P
Oussoren, Esmeralda
van der Ploeg, Ans T
Ruijter, George J G
Schaaf, Gerben
Pijnappel, W W M Pim https://orcid.org/0000-0002-7042-2482
Funding for this research was provided by:
Stichting Metakids (2018-083 and 2021-094)
EMC | Erasmus MC Sophia Kinderziekenhuis (S18-59)
Prinses Beatrix Spierfonds (W.OP20-04)
Hersenstichting (DR-2021-00386)
Stichting Dioraphte (20210367)
For Wishdom Foundation
Nederlandse Organisatie voor Wetenschappelijk Onderzoek (NWA.1389.20.049)
Article History
Received: 10 January 2025
Revised: 12 September 2025
Accepted: 16 September 2025
First Online: 29 September 2025
Disclosure and competing interests statement
: Ans T van der Ploeg (AvdP) has received consulting fees from Sanofi Genzyme and has provided consulting services, participated in advisory boards meetings and received grants for premarketing studies and research from industries via agreements between Erasmus MC and the industry. WWM Pim Pijnappel (WP) is cofounder and scientific advisor of LentiCure.