Khan, Mohammad R A
Garcha, Priya
Lapinska, Viktorija
Nie, Yuanjinze https://orcid.org/0009-0006-4483-7357
Di Girolamo, Ilaria https://orcid.org/0009-0003-4808-0337
Philippeos, Christina https://orcid.org/0000-0001-8654-0291
O’Toole, Edel A
Marshall, John F https://orcid.org/0000-0002-0494-2295
Walko, Gernot https://orcid.org/0000-0002-8504-1738
McGrath, John A
Reynolds, Nick
Watt, Fiona M https://orcid.org/0000-0001-9151-5154
Caley, Matthew https://orcid.org/0000-0003-0504-9922
Rognoni, Emanuel https://orcid.org/0000-0001-6050-2860
Funding for this research was provided by:
Great Ormond Street Hospital for Children (V4622)
DEBRA UK (GR000049)
DEBRA UK (GR000077)
QM | Barts and The London School of Medicine and Dentistry (G-002411)
Article History
Received: 4 July 2025
Revised: 28 May 2026
Accepted: 12 June 2026
First Online: 8 July 2026
Disclosure and competing interests statement
: FMW is an EMBO Molecular Medicine editorial board member and a director of Fibrodyne Ltd.