Sochor, Matthew A.
Vasireddy, Vidyullatha
Drivas, Theodore G.
Wojno, Adam
Doung, Thu
Shpylchak, Ivan
Bennicelli, Jeannette
Chung, Daniel
Bennett, Jean
Lewis, Mitchell
Article History
Received: 14 June 2015
Accepted: 26 October 2015
First Online: 24 November 2015
Competing interests
: J. Bennett, MA. Sochor and M. Lewis are co-inventors on a US provisional patent UPN#Y6194 describing the autogenously regulated expression system. JB and JL Bennicelli (JLB) are co-inventors of US patent # X5873USA_05162011, “Proviral Plasmids for Production of Recombinant Adeno-Associated Virus,” which describes the proviral backbone plasmid used in this study. JB serves on scientific advisory boards for Avalanche Technologies, Spark Therapeutics and Sanofi-Aventis, is a consultant for Novartis and is a founder of GenSight Biologics. The other authors declare that they have no competing interests.