McGovern, Margaret M.
Wasserstein, Melissa P.
Kirmse, Brian
Duvall, W. Lane
Schiano, Thomas
Thurberg, Beth L.
Richards, Susan
Cox, Gerald F.
This article is maintained by: Elsevier
Article Title: Novel first-dose adverse drug reactions during a phase I trial of olipudase alfa (recombinant human acid sphingomyelinase) in adults with Niemann–Pick disease type B (acid sphingomyelinase deficiency)
Journal Title: Genetics in Medicine
CrossRef DOI link to publisher maintained version: https://doi.org/10.1038/gim.2015.24
Content Type: article
Copyright: © 2016, The Author(s), under exclusive licence to the American College of Medical Genetics and Genomics