Hahn, Si Houn
Kronn, David
Leslie, Nancy D.
Pena, Loren D.M.
Tanpaiboon, Pranoot
Gambello, Michael J.
Gibson, James B.
Hillman, Richard
Stockton, David W.
Day, John W.
Wang, Raymond Y.
An Haack, Kristina
Shafi, Raheel
Sparks, Susan
Zhao, Yang
Wilson, Catherine
Kishnani, Priya S.
This article is maintained by: Elsevier
Article Title: Efficacy, safety profile, and immunogenicity of alglucosidase alfa produced at the 4,000-liter scale in US children and adolescents with Pompe disease: ADVANCE, a phase IV, open-label, prospective study
Journal Title: Genetics in Medicine
CrossRef DOI link to publisher maintained version: https://doi.org/10.1038/gim.2018.2
Content Type: article
Copyright: © 2018, The Author(s), under exclusive licence to the American College of Medical Genetics and Genomics