Ameliorating pathogenesis by removing an exon containing a missense mutation: a potential exon-skipping therapy for laminopathies
Crossref DOI link: https://doi.org/10.1038/gt.2015.8
Published Online: 2015-04-02
Published Print: 2015-06
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Scharner, J
Figeac, N
Ellis, J A
Zammit, P S
Text and Data Mining valid from 2015-04-02
Version of Record valid from 2015-04-02
Article History
Received: 9 September 2014
Revised: 18 December 2014
Accepted: 30 December 2014
First Online: 2 April 2015
Competing interests
: The authors declare no conflict of interest.