Polgreen, Lynda E.
Lund, Troy C.
Braunlin, Elizabeth
Tolar, Jakub
Miller, Bradley S.
Fung, Ellen
Whitley, Chester B.
Eisengart, Julie B.
Northrop, Elise
Rudser, Kyle
Miller, Weston P.
Orchard, Paul J.
Article History
Received: 15 January 2019
Revised: 17 May 2019
Accepted: 30 June 2019
First Online: 21 August 2019
Competing interests
: L.E.P. is a speaker and consultant for Sanofi/Genzyme, receives research support from Sanofi/Genzyme and Shire, and is a consultant for Sangamo. T.C.L. receives research support from Sanofi/Genzyme. E.B. is a speaker for Sanofi/Genzyme and receives research support from BioMarin and Bluebird Bio. B.S.M. is a consultant for AbbVie, Ascendis, Ferring, Novo Nordisk, Pfizer, Sandoz and Versartis and has received research support from Alexion, Ascendis, Endo Pharmaceuticals, Genentech, Genzyme, Novo Nordisk, Opko, Sandoz, Sangamo, Shire, Tolmar and Versartis. E.F. is a consultant for BioMarin Pharmaceuticals. C.B.W. is a consultant for Sanofi/Genzyme. J.B.E. has received honoraria, consulting fees, and/or research support from ArmaGen, Regenexbio, Sangamo, and Sanofi/Genzyme, and has done contract work for Shapiro Neuropsychology Consulting, LLC. W.P.M. is an employee of Sangamo Therapeutics. P.J.O. receives research and clinical trial support from Sanofi/Genzyme, Horizon, Magenta and Bluebird Bio. The other authors declare no competing interests.